Children with H-abc need your help! find out more about how you can donate to this cause and help find a cure.
WE ARE STRONGER TOGETHER THAN WE ARE ALONE.
WITH YOUR HELP WE WILL FIND THE CURE
At this time, the team at CHOP is looking at gene therapy to treat H-ABC, as its ability to cure cellular-level diseases is promising. Once they’re able to determine the best approach for gene therapy, they can then get started on obtaining FDA approval and launching a clinical trial.