Great news that Synapix Bio have secured £13.2m to fund clinical trials for H-ABC/Tubb4a!
Oxford biotech firm secures £13.2m to develop first treatment for rare, incurable, deadly disease. (synaptixbio.com)
Great news that Synapix Bio have secured £13.2m to fund clinical trials for H-ABC/Tubb4a!
Virtual Reality for H-abc
Another article about one of our H-abc kids!
NIH, FDA and 15 organisations join forces to increase effective gene therapies for rare diseases.
New Biotech, Synaptix, launched to develop treatment for Tubb4a H-abc!
Darren Hardy the Machine!
5 Marathons in 50 Hours video
5 Marathons in 50 Hours!
H-abc family meeting the Queen of Spain!
BBC Breakfast news interviews H-abc families
ULF H-abc Conference presented by Dr Vanderver
Ben Fogle has given us his Twitter account for a week!
News article in The Sun online!
We now have our Charity Commission number!
Our new Youtube video!
Art Exhibition